News and press releases about the Joshua Frase Foundation and its efforts behind CNM/MTM

Thu, Jul 16, 2020

A Tale of Two Clinical Trials: Gene Therapy for a Rare Disease and a Vaccine for COVID-19

Encouraging preliminary findings in a phase I clinical trial for a COVID-19 vaccine were widely reported as soon as the paper appeared in The New England Journal of Medicine July 14. Coverage of the recent deaths of two boys in a clinical trial to test a gene therapy for a rare, devastating muscle disease were more under-the-radar. Comparing the two very different scenarios illuminates the scientific rigor behind the clinical trial process.